Big News form the Charité


Dear supporters of Maje,
we wish you a happy new year 2021! Better than the last one and above all with more TOGEHTER and less hurdles!

We start optimistically into the new year, because since last week we know that there are first indications of a gene correction on Maje’s cells in the Berlin research laboratory of the Charité! ????????

Grant application rejected

If you have a disease that occurs more frequently, the chances are good that drugs already exist or are (want to) be developed, because from a pharmaceutical company’s point of view, the investment is “worthwhile”.
But people with so-called “rare” diseases also want to benefit from the medical-technical achievements. No human being is “rare”, everyone is unique and everyone has the right to medical care. Research institutions and pharmaceutical companies should think more globally and consider the findings of all research projects as profitable.

At the Charité in Berlin

In July we were allowed to visit the wonderful team around Prof. Dr. Spuler in Berlin and get an insight into their work with muscle cells. The team is working hard to develop a therapy for muscle diseases.